Niemann-Pick Disease

Entity type image
Type: Keyphrase
Name: Niemann-Pick Disease
First reported May 14 2013 - Updated May 14 2013 - 1 reports

Orphan designation: 2-Hydroxypropyl-β-cyclodextrin, for the: Treatment of Niemann-Pick disease type C

[Published Orphan designations - May 14 2013]
First reported May 06 2013 - Updated May 06 2013 - 1 reports

Hundreds turn out for Walk/Run for Kailey to honor girl, fund research

Z 2013-05-05T19:46:26Z Lu Ann Franklin Times Correspondent nwitimes.com3 minutes ago • Lu Ann Franklin Times CorrespondentST. JOHN | Hundreds came together Sunday on the Clark Middle School track for the Walk/Run for Kailey.Scout troops, neighbors, classmates ... [Published NWI Times - May 06 2013]
First reported Jan 24 2013 - Updated Jan 24 2013 - 1 reports

Clinical trial begins for rare and fatal illness nicknamed “childhood Alzheimer’s”

Originally posted on Spoonful of Medicine - a blog from Nature Medicine Addison and Cassidy Hempel  are seven-year-old identical twins who are among only about 500 people in the world with an extremely rare but fatal neurological disease that gradually ... [Published nature.com blogs - Jan 24 2013]

Quotes

...ltoreq.3.0 mg/kg; in fact, clinical symptoms of toxicity were not observed until doses .gtoreq.10 mg/kg were used. See, "Dose Responsive Toxicological Findings Following Intravenous Administration of Recombinant Human Acid Sphingomyelinase (rhASM) to Acid Sphingomyelinase Knock-out (ASMKO) Mice" C Nickerson, J Murray, A Vitsky, M Hawes, S Ryan, P Ewing, B Thurberg, L Andrews. Dept Pharm/Tox, Pathology, Genzyme Corp., Framingham, Mass...
Dose escalation enzyme replacement therapy for treating acid sphingomyelinase deficiency [Published PharmCast - Jan 24 2013]
...Medical Research Institute of Infectious Diseases, has suggested a possible strategy for blocking infection due to Ebola virus, one of the world "s most lethal viruses and a potential bioterrorism agent."
How Ebola virus gains entry into cells and transmits deadly infection [Published Topnews.in - Aug 25 2011]

More Content

All (8) | News (5) | Reports (0) | Blogs (2) | Audio/Video (0) | Fact Sheets (0) | Press Releases (1)
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Orphan designation: 2-Hydroxypropyl-β-cycl... [Published Orphan designations - May 14 2013]
Hundreds turn out for Walk/Run for Kailey to ho... [Published NWI Times - May 06 2013]
Research and Markets: Acid Sphingomyelinase Def... [Published Business Wire Health News - Feb 25 2013]
Clinical trial begins for rare and fatal illnes... [Published nature.com blogs - Jan 24 2013]
Dose escalation enzyme replacement therapy for ... [Published PharmCast - Jan 24 2013]
Differential Diagnosis of Psychotic Symptoms: M... [Published Psychiatric Times - Dec 03 2012]
To the extreme: Memory walk unites families in ... [Published Canton Repository - Aug 18 2012]
How Ebola virus gains entry into cells and tran... [Published Topnews.in - Aug 25 2011]
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Orphan designation: 2-Hydroxypropyl-β-cycl... [Published Orphan designations - May 14 2013]
Clinical trial begins for rare and fatal illnes... [Published nature.com blogs - Jan 24 2013]
Originally posted on Spoonful of Medicine - a blog from Nature Medicine Addison and Cassidy Hempel  are seven-year-old identical twins who are among only about 500 people in the world with an extremely rare but fatal neurological disease that gradually ...
1

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sort by: Date | Relevance
Research and Markets: Acid Sphingomyelinase Def... [Published Business Wire Health News - Feb 25 2013]
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